Budget impact analysis, Medicaid perspective for United States and selected state programs
. | Total no. eligible for gene therapy . | No. eligible for therapy per 100 000 plan enrollees . | No. to receive therapy, year 1 . | Budget impact, year 1 (million USD) . | PMPM cost, year 1 . | % change in year 1 PMPM cost from original model∗ 6 . | PMPM cost, year 5 . |
---|---|---|---|---|---|---|---|
United States† | 7742 | 8.5 | 542 | $1241.0 | $1.13 | 18% | $0.75 |
Alabama | 338 | 29.2 | 24 | $54.2 | $3.90 | 49% | $2.60 |
Washington, DC | 69 | 23.6 | 5 | $11.0 | $3.15 | 45% | $2.10 |
Florida | 904 | 18.7 | 63 | $144.9 | $2.50 | 41% | $1.67 |
Georgia | 720 | 29.3 | 50 | $115.4 | $3.92 | 57% | $2.61 |
Louisiana | 445 | 23.7 | 31 | $71.4 | $3.17 | 46% | $2.11 |
Maryland | 329 | 19.7 | 23 | $52.8 | $2.63 | 59% | $1.75 |
Mississippi | 203 | 26.5 | 14 | $32.5 | $3.55 | –4% | $2.36 |
North Carolina | 409 | 18.1 | 29 | $65.5 | $2.41 | 28% | $1.60 |
South Carolina | 350 | 27.1 | 25 | $56.1 | $3.62 | 43% | $2.42 |
Virginia | 339 | 17.2 | 24 | $54.4 | $2.30 | 20% | $1.54 |
Sample average | 411 | 21.9 | 29 | $65.8 | $3.11 | 40% | $2.08 |
. | Total no. eligible for gene therapy . | No. eligible for therapy per 100 000 plan enrollees . | No. to receive therapy, year 1 . | Budget impact, year 1 (million USD) . | PMPM cost, year 1 . | % change in year 1 PMPM cost from original model∗ 6 . | PMPM cost, year 5 . |
---|---|---|---|---|---|---|---|
United States† | 7742 | 8.5 | 542 | $1241.0 | $1.13 | 18% | $0.75 |
Alabama | 338 | 29.2 | 24 | $54.2 | $3.90 | 49% | $2.60 |
Washington, DC | 69 | 23.6 | 5 | $11.0 | $3.15 | 45% | $2.10 |
Florida | 904 | 18.7 | 63 | $144.9 | $2.50 | 41% | $1.67 |
Georgia | 720 | 29.3 | 50 | $115.4 | $3.92 | 57% | $2.61 |
Louisiana | 445 | 23.7 | 31 | $71.4 | $3.17 | 46% | $2.11 |
Maryland | 329 | 19.7 | 23 | $52.8 | $2.63 | 59% | $1.75 |
Mississippi | 203 | 26.5 | 14 | $32.5 | $3.55 | –4% | $2.36 |
North Carolina | 409 | 18.1 | 29 | $65.5 | $2.41 | 28% | $1.60 |
South Carolina | 350 | 27.1 | 25 | $56.1 | $3.62 | 43% | $2.42 |
Virginia | 339 | 17.2 | 24 | $54.4 | $2.30 | 20% | $1.54 |
Sample average | 411 | 21.9 | 29 | $65.8 | $3.11 | 40% | $2.08 |