Table 1.

Patient characteristics at presentation

Baseline characteristicsCaplacizumab cohort
 N = 16, 100% 
Age, median (range), mo 14 y and 9 mo (2 y 9 mo to 17 y 17 mo) 
Body weight, kg, median (range) 63.2 (15.3-101) 
Sex  
Male 
Female 10 
Ethnicity  
Black 
White 
Asian 
Mixed race 
Clinical features  
Neurological symptoms at presentation 10 
Confusion  
Headache 5 (including agitation in 1)
5 (including memory loss in 1) 
Intensive care 
Patients requiring intubation 
Baseline characteristicsCaplacizumab cohort
 N = 16, 100% 
Age, median (range), mo 14 y and 9 mo (2 y 9 mo to 17 y 17 mo) 
Body weight, kg, median (range) 63.2 (15.3-101) 
Sex  
Male 
Female 10 
Ethnicity  
Black 
White 
Asian 
Mixed race 
Clinical features  
Neurological symptoms at presentation 10 
Confusion  
Headache 5 (including agitation in 1)
5 (including memory loss in 1) 
Intensive care 
Patients requiring intubation 
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