Table 1.

Patient demographic and baseline disease characteristics

Baseline characteristics, (N = 12)
Age, median (range) y 41.5 (27-66) 
Sex, female, n (%) 9 (75.0) 
Race, n (%)  
White 8 (66.7) 
Black or African American 3 (25.0) 
Asian 1 (8.3) 
Weight, kg [n = 11], mean (range) 78.3 (57-114) 
Disease duration at screening, y [n = 7], median (range) 4.7 (2.0-36.4) 
Platelet count, median (range), ×109/L 19 (1-57) 
Number of prior treatments, median (range) 5.5 (2-10) 
Prior treatment received, n (%)  
Rituximab 10 (83.3) 
Corticosteroids 8 (66.7) 
TPO-RA  
Romiplostim 8 (66.7) 
Eltrombopag 8 (66.7) 
IVIg 7 (58.3) 
Fostamatinib 2 (16.7) 
Rilzabrutinib  1 (8.3) 
Prior splenectomy, n (%) 4 (33.3) 
Baseline characteristics, (N = 12)
Age, median (range) y 41.5 (27-66) 
Sex, female, n (%) 9 (75.0) 
Race, n (%)  
White 8 (66.7) 
Black or African American 3 (25.0) 
Asian 1 (8.3) 
Weight, kg [n = 11], mean (range) 78.3 (57-114) 
Disease duration at screening, y [n = 7], median (range) 4.7 (2.0-36.4) 
Platelet count, median (range), ×109/L 19 (1-57) 
Number of prior treatments, median (range) 5.5 (2-10) 
Prior treatment received, n (%)  
Rituximab 10 (83.3) 
Corticosteroids 8 (66.7) 
TPO-RA  
Romiplostim 8 (66.7) 
Eltrombopag 8 (66.7) 
IVIg 7 (58.3) 
Fostamatinib 2 (16.7) 
Rilzabrutinib  1 (8.3) 
Prior splenectomy, n (%) 4 (33.3) 

Average of all platelet counts at screening, including day 0.

Investigational Bruton’s tyrosine kinase inhibitor.

Close Modal

or Create an Account

Close Modal
Close Modal