Table 1.

Baseline characteristics of patients who received transplant

Total (N = 27),
n (%)
Sex  
Female 13 (48) 
Male 14 (52) 
Race and ethnicity  
Non-Hispanic White 17 (63) 
Hispanic White 
Non-Hispanic Black 5 (19) 
Hispanic Black 1 (3) 
Asian/Pacific Islander 3 (11) 
Native American 
>1 race 1 (3) 
Unknown 
Age, y  
Mean (SD) 32 (19) 
Median (range) 25 (3-63) 
Age, y  
<10 
10-19 
20-29 
30-39 
40-49 
50-59 
60-69 
Very severe AA diagnosis (ANC <0.2 × 109/L) 14 (52) 
SAA diagnosis (ANC <0.5 × 109/L) 13 (48) 
Clonality at baseline (PNH clone or molecular data including karyotype) 22 (81) 
Documented inherited predisposition to AA 1 (3) 
Interval from diagnosis to transplant, d  
Mean (SD) 91 (55) 
Median (range) 78 (12-249) 
Donor age, y  
Mean (SD) 33 (12) 
Median (range) 30 (13-56) 
Donor relationship  
Haplo sibling 7 (26) 
Haplo parent 6 (22) 
Haplo child 7 (26) 
Haplo second-degree relative (cousin, niece, or nephew) 7 (26) 
Donor sex  
Female 16 (59) 
Male 11 (41) 
Total (N = 27),
n (%)
Sex  
Female 13 (48) 
Male 14 (52) 
Race and ethnicity  
Non-Hispanic White 17 (63) 
Hispanic White 
Non-Hispanic Black 5 (19) 
Hispanic Black 1 (3) 
Asian/Pacific Islander 3 (11) 
Native American 
>1 race 1 (3) 
Unknown 
Age, y  
Mean (SD) 32 (19) 
Median (range) 25 (3-63) 
Age, y  
<10 
10-19 
20-29 
30-39 
40-49 
50-59 
60-69 
Very severe AA diagnosis (ANC <0.2 × 109/L) 14 (52) 
SAA diagnosis (ANC <0.5 × 109/L) 13 (48) 
Clonality at baseline (PNH clone or molecular data including karyotype) 22 (81) 
Documented inherited predisposition to AA 1 (3) 
Interval from diagnosis to transplant, d  
Mean (SD) 91 (55) 
Median (range) 78 (12-249) 
Donor age, y  
Mean (SD) 33 (12) 
Median (range) 30 (13-56) 
Donor relationship  
Haplo sibling 7 (26) 
Haplo parent 6 (22) 
Haplo child 7 (26) 
Haplo second-degree relative (cousin, niece, or nephew) 7 (26) 
Donor sex  
Female 16 (59) 
Male 11 (41) 

AA, aplastic anemia; haplo; haploidentical; SD, standard deviation.

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