Baseline characteristics with respect to the outcome of the patients
. | Overall Median (IQR) . | Good responder (n = 89) Median (IQR) . | Responder (n = 16) Median (IQR) . | Nonresponder (n = 30) Median (IQR) . | P . |
---|---|---|---|---|---|
Age, y | 6 (3-10) | 5 (3-8.5) | 6.5 (3.2-10.7) | 7 (3-12.2) | .101∗ |
Weight, kg | 17 (12-24) | 16 (11.2-22) | 20 (16.2-26.5) | 20 (12-33) | .075∗ |
Age at first transfusion, mo | 9 (6-15) | 9 (6-14) | 7.5 (3.2-1.6) | 9 (5.7-1.4) | .824∗ |
Age at the start of HU, y | 1.2 (0.9-2.5) | 1 (0.9-2) | 2.1 (1-4.8) | 1.6 (0.8-4) | .252∗ |
HbA electrophoresis, n = 12 | 5.7 (2.4-11.2) | 3.2 (2.1-10.8) | 6.6 (6.6-6.6) | 7.8 (5.1-7.8) | .392∗ |
HbA2 electrophoresis, n = 45 | 2.6 (2-4.1) | 2.8 (2.2-4) | 2.3 (1.3-4.1) | 2.2 (1.6-4.2) | .606∗ |
HbF electrophoresis, n = 76 | 96.4 (94-98) | 96.6 (94.1-97.9) | 96.2 (60.8-97.7) | 96.3 (92.7-97.8) | .851∗ |
. | Overall Median (IQR) . | Good responder (n = 89) Median (IQR) . | Responder (n = 16) Median (IQR) . | Nonresponder (n = 30) Median (IQR) . | P . |
---|---|---|---|---|---|
Age, y | 6 (3-10) | 5 (3-8.5) | 6.5 (3.2-10.7) | 7 (3-12.2) | .101∗ |
Weight, kg | 17 (12-24) | 16 (11.2-22) | 20 (16.2-26.5) | 20 (12-33) | .075∗ |
Age at first transfusion, mo | 9 (6-15) | 9 (6-14) | 7.5 (3.2-1.6) | 9 (5.7-1.4) | .824∗ |
Age at the start of HU, y | 1.2 (0.9-2.5) | 1 (0.9-2) | 2.1 (1-4.8) | 1.6 (0.8-4) | .252∗ |
HbA electrophoresis, n = 12 | 5.7 (2.4-11.2) | 3.2 (2.1-10.8) | 6.6 (6.6-6.6) | 7.8 (5.1-7.8) | .392∗ |
HbA2 electrophoresis, n = 45 | 2.6 (2-4.1) | 2.8 (2.2-4) | 2.3 (1.3-4.1) | 2.2 (1.6-4.2) | .606∗ |
HbF electrophoresis, n = 76 | 96.4 (94-98) | 96.6 (94.1-97.9) | 96.2 (60.8-97.7) | 96.3 (92.7-97.8) | .851∗ |
. | n (%) . | n (%) . | n (%) . | n (%) . | . |
---|---|---|---|---|---|
Sex | |||||
Male | 77 (57) | 42 (47.2) | 6 (37.5) | 10 (33.3) | .372† |
Female | 58 (43) | 47 (52.8) | 10 (62.5) | 20 (66.7) |
. | n (%) . | n (%) . | n (%) . | n (%) . | . |
---|---|---|---|---|---|
Sex | |||||
Male | 77 (57) | 42 (47.2) | 6 (37.5) | 10 (33.3) | .372† |
Female | 58 (43) | 47 (52.8) | 10 (62.5) | 20 (66.7) |