Table 1.

Study population characteristics

CharacteristicN = 33*
Age at start of TVTC, y 11.0 (1-24) 
Sex 
 Female 17 (51.5) 
 Male 16 (48.5) 
BM blasts, % 32 (10-99) 
Prior HSCT 
 No 24 (72.7) 
 Yes 9 (27.3) 
Prior anthracycline (cumulative dose, mg/m2342 (60-492) 
Group A n = 14 
 Length of CR1, d 
   <180 1 (7.1) 
   180-365 6 (50) 
   >365 7 (42.9) 
 Prior HSCT 4 (28.6) 
Group B n = 19 
 Prior HSCT 5 (26.3) 
CharacteristicN = 33*
Age at start of TVTC, y 11.0 (1-24) 
Sex 
 Female 17 (51.5) 
 Male 16 (48.5) 
BM blasts, % 32 (10-99) 
Prior HSCT 
 No 24 (72.7) 
 Yes 9 (27.3) 
Prior anthracycline (cumulative dose, mg/m2342 (60-492) 
Group A n = 14 
 Length of CR1, d 
   <180 1 (7.1) 
   180-365 6 (50) 
   >365 7 (42.9) 
 Prior HSCT 4 (28.6) 
Group B n = 19 
 Prior HSCT 5 (26.3) 

Group A = first relapse; Group B = second or greater R/R/primary refractory.

*

Statistics presented as median (minimum-maximum) or n (%).

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